Publications &
Presentations
In our pursuit of scientific advancement we are committed to sharing our acquired knowledge through actively publishing our data in peer-reviewed journals and academic conferences. We aim to provide a deeper understanding through extensive study and analysis on ileal bile acid transporter (IBAT) inhibition, for both the scientific and patient communities.
Research Updates
Featured Presentations & Publications
Efficacy and safety of maralixibat in patients with progressive familial intrahepatic cholestasis (MARCH-PFIC): a randomized placebo-controlled phase 3 study
Thompson, et al. Oral Presentation, AASLD 2022.
Safety and tolerability characterization of maralixibat in infants with ALGS from 2 months of age: Interim results from the RISE study
Gonzales, et al. Poster Presentation, AASLD 2022.
Real-world safety experience in patients with Alagille syndrome treated with maralixibat
Himes, et al. Poster Presentation, AASLD 2022.
Maralixibat-treated patients with Alagille syndrome demonstrate improved event-free survival in a natural history comparison with patients from the GALA database: application of real-world evidence analytics
Kamath, et al. Poster Presentation, NASPGHAN 2022.
Maralixibat treatment response in Alagille syndrome is associated with improved health-related quality of life
Kamath BM, et al. The Journal of Pediatrics. 2022; ISSN 0022-3476.
Latest Research Updates
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- Alagille syndrome
- Biliary atresia
- Health economics and outcomes research
- IBAT inhibition
- LIVMARLI (maralixibat)
- Patient-reported outcomes validation
- Primary biliary cholangitis
- Primary sclerosing cholangitis
- Progressive familial intrahepatic cholestasis
- Volixibat
Until a relevant regulatory agency has approved a Mirum product for a specific disease or population, any scientific presentations regarding such disease or population are not to be considered instruction on the appropriate use of Mirum products or clinical candidates.
